TrialSignal
Clinical trial intelligence report
A Phase 2, Open-label, Sequential Cohort Dose-escalation Study of BMN 111 in Children With Achondroplasia
Source-linked diligence brief with registry provenance, taxonomy normalization and premium analytical context.
Generated
Jun 13, 2026
NCT ID
NCT02055157
Status
COMPLETED
Phase
PHASE2
Sponsor
BioMarin Pharmaceutical
Executive brief
Investment-Ready Snapshot
This is a Phase 2, open-label, sequential cohort dose-escalation study of BMN 111 in children with achondroplasia. The primary objective is to assess the safety and tolerability of daily BMN 111 administered to children with achondroplasia.
Source & freshness
Provenance
https://clinicaltrials.gov/study/NCT02055157
Indication
Achondroplasia
Modality
small molecule
Target
BMN 111
Intervention
BMN 111
Source record
Protocol Description
Detailed source ingestion pending.
Source record
Outcome Measures
Detailed source ingestion pending.
Source record
Eligibility
Detailed source ingestion pending.
AI analysis
Known Results And Readout Context
Detailed source ingestion pending.
IP intelligence
Patent And IP Landscape
Detailed source ingestion pending.
Source record
Contacts
Detailed source ingestion pending.