TrialSignal
Clinical trial intelligence report
Phase I/II Trial of Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy Type I (CARNI-VAL Type I)
Source-linked diligence brief with registry provenance, taxonomy normalization and premium analytical context.
Generated
Jul 28, 2026
Report code
NCT00661453-Jul 28, 2026
NCT ID
NCT00661453
Status
COMPLETED
Phase
PHASE1
Sponsor
University of Utah
Executive brief
Investment-Ready Snapshot
Phase I/II Trial of Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy Type I (CARNI-VAL Type I) is a PHASE1 clinical asset sponsored by University of Utah in Spinal Muscular Atrophy Type I. SEO and diligence focus: Valproic Acid and Levocarnitine, endpoint relevance, enrollment feasibility, competitive positioning, readout timing and IP durability.
Source & freshness
Provenance
https://clinicaltrials.gov/study/NCT00661453
Indication
Spinal Muscular Atrophy Type I
Modality
small molecule
Target
Valproic Acid and Levocarnitine
Intervention
Valproic Acid and Levocarnitine
Source record
Protocol Description
Detailed source ingestion pending.
Source record
Outcome Measures
Detailed source ingestion pending.
Source record
Eligibility
Detailed source ingestion pending.
AI analysis
Known Results And Readout Context
Detailed source ingestion pending.
IP intelligence
Patent And IP Landscape
Detailed source ingestion pending.
Source record
Contacts
Detailed source ingestion pending.